Soleno Therapeutics is nearing FDA approval for its lead drug, DCCR, targeting Prader-Willi Syndrome, a rare genetic ...

Alnylam Pharmaceuticals' shares rose about 7% before the bell on Friday following U.S. approval for its drug for a rare and deadly heart disease, securing an entry into a market dominated by Pfizer's ...

(Reuters) -Gene therapy, with its offer of a possible cure for rare diseases like sickle cell, is losing early investors to ...

A cat has nine lives, but I believe that I have more. While I can’t remember the exact date that I started feeling sick, I have struggled with fatigue for a long time. I thought it was just that, a ...

An experimental treatment appears to delay Alzheimer’s symptoms in some people genetically destined to get the disease in ...

Encelto is small, semi-permeable capsule implanted in the eye that contains allogeneic retinal pigment epithelium cells ...

An experimental treatment appears to delay Alzheimer’s symptoms in some people genetically destined to get the disease in their 40s or 50s, according to new findings from ongoing research now caught ...

Art and science are disciplines that have historically co-existed as polarised entities. However, artists and scientists both ...

While some bat species have seen up to a 99% population decline, Rafinesque's big-eared bat has shown a strong resistance to ...

A local family said they now have important answers about their daughter thanks to the work of the Indiana University Rare ...