News

Researchers identified a unique protein signature in the blood of BMD and LGMD patients that may reflect disease progression.
Ifetroban improved heart function and reduced cardiac damage biomarkers in people with DMD in a Phase 2 clinical trial.
Summer can be rough for folks with muscular dystrophy, columnist Patrick Moeschen writes, but it can also bring adventures in appreciation.
The FDA has granted rare pediatric disease designation to PBGENE-DMD, an experimental gene-editing therapy for Duchenne ...
The U.S. Food and Drug Administration is due to review data on deramiocel, a cell therapy up for approval for heart disease ...
A recent dream leaves columnist Robin Stemple questioning how his disability progression due to FSHD affects his family and ...
Columnist Betty Vertin is grateful to have the help of a hired caregiver, but it's also been a difficult adjustment, she says.
Marisa holds a Master of Science in cellular and molecular pathology from the University of Pittsburgh, where she studied novel genetic drivers of ovarian cancer. Her areas of expertise include cancer ...
A recent concert in Singapore was all about finding harmony through the talents that unite us in life, writes columnist.
Doctors can use several tests to diagnose muscular dystrophy (MD). A correct diagnosis gives patients an understanding of how their disease is likely to progress. It also helps doctors do a better job ...
Becker muscular dystrophy is a condition in which skeletal and heart muscles slowly degrade. The causes and symptoms of Becker are similar to those of Duchenne muscular dystrophy, though the disease’s ...